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Clinical research blog

Explore our blog for insights into the big questions in precision medicine and clinical research.

From fragmentation to fusion: How AI is unlocking the value of multi-omic data in drug discovery

In drug discovery, data is the key to success. Although more and more large-scale data is being generated every year, much of it is inaccessible or fragmented. ...
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Podcast recap: Justin Porcano on speeding up treatments for Usher syndrome type 1B

In the last episode of The Genetics Podcast, Patrick spoke with Justin Porcano, co-founder and executive director of Save Sight Now, a nonprofit accelerating th...
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Scaling the promise of gene editing: Why progress still falls short of potential

Gene editing has progressed significantly over the past decade, evolving from an experimental technology that was associated with safety and efficacy limitation...
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Podcast recap: Chris Hopkins on developing a one-time cell therapy for Fabry disease

On this episode of The Genetics Podcast, Patrick spoke with Chris Hopkins, CEO of Glafabra Therapeutics, a company developing a one-time autologous cell therapy...
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Innovation in AAV: Breaking through bottlenecks in yield, safety, and cost

At this year’s European Society of Gene & Cell Therapy (ESGCT) meeting, one theme resonated across sessions: adeno-associated viruses (AAVs) are entering a ...
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Podcast recap: The state of AAV gene therapy and where it’s headed

On the most recent episode of The Genetics Podcast, host Patrick Short took a solo deep dive into gene therapy, with a focus on therapies based on delivery via ...
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Podcast recap: Sonya Dumanis and Andy Singleton on building a global genetics engine for Parkinson’s

On the most recent episode of The Genetics Podcast, we hosted Sonya Dumanis and Andy Singleton to unpack GP2, the Global Parkinson’s Genetics Program. GP2 is a ...
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Clinical trial site partnerships in 2025: What sponsors need to know

At the Partnerships with Sites summit in September 2025, new data from the Tufts Center for the Study of Drug Development (Tufts CSDD) underscored how the globa...
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Podcast recap: Wanda Smith on turning a family diagnosis into CureGRN

In last week’s episode of The Genetics Podcast, Patrick Short sat down with Wanda Smith, founder of CureGRN and long-time advocate for families affected by prog...
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Podcast recap: Terry Pirovolakis on turning his son’s diagnosis into Elpida Therapeutics

On the most recent episode of The Genetics Podcast, we hosted Terry Pirovolakis, founder and CEO of Elpida Therapeutics. Terry’s journey began the day his young...
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