Gene and cell therapies represent a fundamental shift in how rare diseases are treated. Rather than managing symptoms, these therapies target the underlying gen...
Continue reading
Rare disease drug development operates under a unique set of structural constraints. Patient populations are small and dispersed, diagnostic timelines are long,...
Continue reading
In a recent episode of The Genetics Podcast, Patrick Short hosted Dr. Nessan Bermingham, a scientist turned biotech entrepreneur and operating partner at Khosla...
Continue reading
There are a number of innovative tools and technologies which are enabling precision patient finding. From AI to e-consent, here we explore how they are changin...
Continue reading
In the latest episode of The Genetics Podcast, Patrick Short was joined by Dr. Luis Diaz, head of the Division of Solid Tumor Oncology at Memorial Sloan Ketteri...
Continue reading
On a recent episode of The Genetics Podcast, Patrick Short speaks with Dr. Susan Liebman, a professor emerita and researcher, about her personal and professiona...
Continue reading
Precision patient finding has the potential to radically reduce the cost of trials and create a more centralized approach which serves to benefit a multitude of...
Continue reading
Clinical trials are essential for bringing new treatments to patients, but they’re not without challenges. Recruiting the right participants, staying on budget,...
Continue reading
Precision patient finding is an evolving field that is growing in line with the demands of precision medicine and rare disease research. Unlike traditional pati...
Continue reading
Implementing precision neurology comes with its own set of complexities—from decoding the brain's intricate workings to addressing the ethical challenges of usi...
Continue reading