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Clinical research blog

Explore our blog for insights into the big questions in precision medicine and clinical research.

From fragmentation to fusion: How AI is unlocking the value of multi-omic data in drug discovery

In drug discovery, data is the key to success. Although more and more large-scale data is being generated every year, much of it is inaccessible or fragmented. ...
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Podcast recap: Justin Porcano on speeding up treatments for Usher syndrome type 1B

In the last episode of The Genetics Podcast, Patrick spoke with Justin Porcano, co-founder and executive director of Save Sight Now, a nonprofit accelerating th...
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Scaling the promise of gene editing: Why progress still falls short of potential

Gene editing has progressed significantly over the past decade, evolving from an experimental technology that was associated with safety and efficacy limitation...
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Podcast recap: Heidi Rehm and Slavé Petrovski live from ASHG on breaking barriers in genomics

In a special live episode of The Genetics Podcast, recorded at the American Society of Human Genetics (ASHG) meeting, host Patrick Short was joined by two of th...
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Podcast recap: Chris Hopkins on developing a one-time cell therapy for Fabry disease

On this episode of The Genetics Podcast, Patrick spoke with Chris Hopkins, CEO of Glafabra Therapeutics, a company developing a one-time autologous cell therapy...
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Innovation in AAV: Breaking through bottlenecks in yield, safety, and cost

At this year’s European Society of Gene & Cell Therapy (ESGCT) meeting, one theme resonated across sessions: adeno-associated viruses (AAVs) are entering a ...
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Closing the communication gap: A sponsor’s guide to building patient trust and retention

Participation in clinical trials can be burdensome and disruptive. In addition to practical inconveniences and discomfort, participants may have to take time of...
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Podcast recap: The state of AAV gene therapy and where it’s headed

On the most recent episode of The Genetics Podcast, host Patrick Short took a solo deep dive into gene therapy, with a focus on therapies based on delivery via ...
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Expediting study start-up: Best practices for sponsors

Study start-up is a critical stage of the drug development process and can have a major impact on trial timelines, budgets, and overall success. Start-up activi...
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Podcast recap: Sonya Dumanis and Andy Singleton on building a global genetics engine for Parkinson’s

On the most recent episode of The Genetics Podcast, we hosted Sonya Dumanis and Andy Singleton to unpack GP2, the Global Parkinson’s Genetics Program. GP2 is a ...
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