Rare Disease Day 2026 webinar

Turning precision medicine into reality

Precision medicine has delivered breakthroughs in rare disease. But for most patients, access still lags behind innovation.

In this Rare Disease Day panel, leaders across biotech, clinical research, and patient advocacy share what it will take to turn scientific progress into real-world impact.

This on-demand webinar explores how we move beyond promising data toward therapies that are designed with patients, built for scalability, and accessible in practice. Hear from:

• Dr. Patrick Short, CEO and Co-Founder, Sano Genetics (moderator)
• Jimi Olaghere, patient advocate for sickle cell disease and entrepreneur
• Rachel Parexel, Vice President and Head of rare and genetic diseases at Parexel
• Lindsey Wahlstrom, Co-Founder and Chief Momatologist of Rona’s FUN LAB
  

What you will learn:

✅ How lived experience should shape trial design from day one
✅ Why many advanced therapies struggle after approval
✅ The regulatory and payer realities influencing rare disease programs
✅ How to balance scientific rigor with urgency for families
✅ What success should look like in the next five years

If you are developing, funding, or supporting rare disease programs, this discussion will sharpen how you think about evidence, access, and long-term impact.

Watch the recording now.